基因编辑仓鼠Replacing acid alpha-glucosidase in Pompe disease: recombinant and transgenic enzymes are equipotent, but neither completely clears glycogen from type II muscle fibers.
期刊:Molecular therapy : the journal of the American Society of Gene Therapy发表年份:2005作者:Nina Raben; Tokiko Fukuda; Abigail L Gilbert; Deborah de Jong; Beth L Thurberg; Robert J Mattaliano; Peter Meikle; John J Hopwood; Kunio Nagashima; Kanneboyina Nagaraju; Paul H Plotz
