药效评价Recombinant encapsulated cells overexpressing alpha-L-iduronidase correct enzyme deficiency in human mucopolysaccharidosis type I cells.
期刊:Cells, tissues, organs发表年份:2012作者:Guilherme Baldo; Fabiana Quoos Mayer; Maira Burin; Joaquín Carrillo-Farga; Ursula Matte; Roberto Giugliani
